Amicus Clinical Trial

A clinical study or observational registry sponsored or run by Amicus Therapeutics.

BiotechnologyPharmaceuticalsRare DiseasesGenetic DiseasesFabry DiseasePompe DiseaseLysosomal Storage DisordersEnzyme Replacement TherapyPharmacological ChaperonesClinical ResearchLife SciencesPatient Advocacy

Properties

Name	Type	Description
trialId	string	Internal Amicus trial identifier (e.g., AT1001-025, ATB200-08)
name	string	Public name of the study (e.g., ROSSELLA, ZIP, ACTION3)
nctId	string	ClinicalTrials.gov registry identifier
indication	string	Disease indication under study (e.g., Fabry disease, Pompe disease, FSGS)
studyType	string
phase	string
ageRange	object	Eligible age range
investigationalProduct	string	Name or code of the candidate therapy being evaluated
status	string
registryEUPAS	string	EU PAS Register identifier where applicable

View JSON Schema on GitHub

JSON Schema

{
  "$schema": "https://json-schema.org/draft/2020-12/schema",
  "$id": "https://api-evangelist.github.io/amicus-therapeutics/json-schema/amicus-clinical-trial-schema.json",
  "title": "Amicus Clinical Trial",
  "description": "A clinical study or observational registry sponsored or run by Amicus Therapeutics.",
  "type": "object",
  "required": ["trialId", "name", "indication"],
  "properties": {
    "trialId": {
      "type": "string",
      "description": "Internal Amicus trial identifier (e.g., AT1001-025, ATB200-08)"
    },
    "name": {
      "type": "string",
      "description": "Public name of the study (e.g., ROSSELLA, ZIP, ACTION3)"
    },
    "nctId": {
      "type": "string",
      "pattern": "^NCT[0-9]{8}$",
      "description": "ClinicalTrials.gov registry identifier"
    },
    "indication": {
      "type": "string",
      "description": "Disease indication under study (e.g., Fabry disease, Pompe disease, FSGS)"
    },
    "studyType": {
      "type": "string",
      "enum": ["Interventional", "Observational", "Registry", "Expanded Access"]
    },
    "phase": {
      "type": "string",
      "enum": [
        "Phase 1",
        "Phase 2",
        "Phase 3",
        "Phase 4",
        "Not Applicable"
      ]
    },
    "ageRange": {
      "type": "object",
      "properties": {
        "minimumAge": { "type": "string" },
        "maximumAge": { "type": "string" }
      },
      "description": "Eligible age range"
    },
    "investigationalProduct": {
      "type": "string",
      "description": "Name or code of the candidate therapy being evaluated"
    },
    "status": {
      "type": "string",
      "enum": ["Recruiting", "Active", "Completed", "Suspended", "Terminated", "Withdrawn"]
    },
    "registryEUPAS": {
      "type": "string",
      "description": "EU PAS Register identifier where applicable"
    }
  },
  "additionalProperties": false
}