Example Amicus medicine record for Pombiliti (cipaglucosidase alfa-atga), the enzyme replacement component of the two-component Pombiliti + Opfolda regimen for adults with late-onset Pompe disease.
Amicus Pombiliti Medicine Example is an example object payload from Amicus Therapeutics, with 2 top-level fields. It illustrates the shape of data this provider's APIs accept or return.
{
"description": "Example Amicus medicine record for Pombiliti (cipaglucosidase alfa-atga), the enzyme replacement component of the two-component Pombiliti + Opfolda regimen for adults with late-onset Pompe disease.",
"medicine": {
"medicineId": "amx-med-pombiliti",
"brandName": "Pombiliti",
"genericName": "cipaglucosidase alfa-atga",
"drugClass": "Enzyme Replacement Therapy",
"routeOfAdministration": "Intravenous",
"indication": "Late-onset Pompe disease",
"patientPopulation": "Adults with late-onset Pompe disease (LOPD) weighing 88 lbs or more who are not improving on their current enzyme replacement therapy",
"combinationWith": ["Opfolda"],
"mechanismOfAction": "Bis-M6P-enriched ERT designed to deliver active GAA enzyme directly to muscle cells for improved binding and effective uptake",
"approvals": [],
"productSite": "https://www.pombilitiopfolda.com"
}
}
Discovery needs no key. Ratings and market analysis are Pro.
Get an API key
Free tier, no form to fill in. Signing in shares your email address with us — we
store it to create your key and to recognise you if you sign in with another
provider. See our Privacy Policy and
Terms.