amicus-therapeutics · Example Payload

Amicus Galafold Medicine Example

Example Amicus medicine record for Galafold (migalastat), Amicus's first-and-only oral therapy for adults with Fabry disease who have an amenable GLA variant.

BiotechnologyPharmaceuticalsRare DiseasesGenetic DiseasesFabry DiseasePompe DiseaseLysosomal Storage DisordersEnzyme Replacement TherapyPharmacological ChaperonesClinical ResearchLife SciencesPatient Advocacy

Amicus Galafold Medicine Example is an example object payload from amicus-therapeutics, with 2 top-level fields. It illustrates the shape of data this provider's APIs accept or return.

Top-level fields

descriptionmedicine

Example Payload

{
  "description": "Example Amicus medicine record for Galafold (migalastat), Amicus's first-and-only oral therapy for adults with Fabry disease who have an amenable GLA variant.",
  "medicine": {
    "medicineId": "amx-med-galafold",
    "brandName": "Galafold",
    "genericName": "migalastat",
    "drugClass": "Pharmacological Chaperone",
    "routeOfAdministration": "Oral",
    "indication": "Fabry disease",
    "patientPopulation": "Adults with Fabry disease who have a GLA gene variant that is responsive (amenable) to Galafold",
    "combinationWith": [],
    "mechanismOfAction": "Selective, reversible binding to amenable mutant forms of alpha-galactosidase A to stabilize the enzyme, facilitate lysosomal trafficking, and restore activity",
    "approvals": [
      {
        "region": "EU",
        "agency": "European Commission",
        "approvalDate": "2016-05-26"
      }
    ],
    "productSite": "https://www.galafold.com"
  }
}